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Mashup Score: 53
Base editors can correct disease-causing genetic variants. After a neonate had received a diagnosis of severe carbamoyl-phosphate synthetase 1 deficiency, a disease with an estimated 50% mortality …
Source: www.nejm.orgCategories: General Medicine News, General Journals & SocietTweet
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Mashup Score: 12025 June Medical Meeting Report - 1 month(s) ago
The recently concluded American Society of Gene and Cell Therapy (ASGCT) 28th Annual Meeting (New Orleans, May 13-17) showcased ongoing innovations and clinical advances that are helping to realize the full potential of precision genetic and cellular medicines. The FINN Health Strategic Scientific Communications (SSC) team took a deep dive into the more than 2,000 abstracts included in this year’s meeting to identify major trends as well as exciting data sets that demonstrate important progress toward
Source: go.finnpartners.comCategories: General Medicine News, Future of MedicineTweet-
Wow - this is an excellent wrap on the most important things coming out of #ASGCT2025. @FINNPartners has a lot of VERY smart people adding their expertise: https://t.co/EXtX6XFHzz
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Mashup Score: 1Gene therapy delivery system successfully targets CD90+ hematopoietic stem cells in vivo - 2 month(s) ago
Researchers in the lab of Hans-Peter Kiem, MD, PhD, at Fred Hutch Cancer Center have devised a method that could one day treat genetic hematologic disorders by correcting how the body makes blood cells.
Source: www.fredhutch.orgCategories: General Medicine NewsTweet-
Researchers in @HPKiem's lab at Fred Hutch devised a method that could one day treat genetic hematologic disorders by correcting how the body makes blood cells. Read more about their work, which they presented recently at #ASGCT2025. https://t.co/NQzfM1vm4J
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Mashup Score: 1Gene therapy delivery system successfully targets CD90+ hematopoietic stem cells in vivo - 2 month(s) ago
Researchers in the lab of Hans-Peter Kiem, MD, PhD, at Fred Hutch Cancer Center have devised a method that could one day treat genetic hematologic disorders by correcting how the body makes blood cells.
Source: www.fredhutch.orgCategories: General Medicine NewsTweet-
Researchers in @HPKiem's lab at Fred Hutch devised a method that could one day treat genetic hematologic disorders by correcting how the body makes blood cells. Read more about their work, which they presented recently at #ASGCT2025. https://t.co/NQzfM1vm4J
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Mashup Score: 1Gene therapy delivery system successfully targets CD90+ hematopoietic stem cells in vivo - 2 month(s) ago
Researchers in the lab of Hans-Peter Kiem, MD, PhD, at Fred Hutch Cancer Center have devised a method that could one day treat genetic hematologic disorders by correcting how the body makes blood cells.
Source: www.fredhutch.orgCategories: General Medicine NewsTweet-
Researchers in @HPKiem's lab at Fred Hutch devised a method that could one day treat genetic hematologic disorders by correcting how the body makes blood cells. Read more about their work, which they presented recently at #ASGCT2025. https://t.co/NQzfM1vm4J
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Mashup Score: 53
Base editors can correct disease-causing genetic variants. After a neonate had received a diagnosis of severe carbamoyl-phosphate synthetase 1 deficiency, a disease with an estimated 50% mortality …
Source: www.nejm.orgCategories: General Medicine News, General Journals & SocietTweet-
Presented at #ASGCT2025: A lipid nanoparticle–delivered base-editing therapy was custom designed for an infant with a ureacycle disorder. The affected infant was treated at approximately 7 and 8 months of age. Read the Brief Report: https://t.co/EtnnBhGfqi Editorial: https://t.co/56A43OZuy2
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Mashup Score: 71
In this editorial, the authors describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder.
Source: www.nejm.orgCategories: General Medicine News, General Journals & SocietTweet-
In a new editorial, @AndreaGropman, MD, and Alexis C. Komor, PhD (@KomorLab), describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder. Read the editorial: https://t.co/DGBBKbEX2r #ASGCT2025 | @ASGCTherapy https://t.co/Uq6WY3uQix
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Mashup Score: 54
Base editors can correct disease-causing genetic variants. After a neonate had received a diagnosis of severe carbamoyl-phosphate synthetase 1 deficiency, a disease with an estimated 50% mortality …
Source: www.nejm.orgCategories: General Medicine News, General Journals & SocietTweet-
Presented at #ASGCT2025: A lipid nanoparticle–delivered base-editing therapy was custom designed for an infant with a ureacycle disorder. The affected infant was treated at approximately 7 and 8 months of age. Read the Brief Report: https://t.co/EtnnBhGfqi Editorial: https://t.co/56A43OZuy2
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Mashup Score: 71
In this editorial, the authors describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder.
Source: www.nejm.orgCategories: General Medicine News, General Journals & SocietTweet-
In a new editorial, @AndreaGropman, MD, and Alexis C. Komor, PhD (@KomorLab), describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder. Read the editorial: https://t.co/DGBBKbEX2r #ASGCT2025 | @ASGCTherapy https://t.co/Uq6WY3uQix
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Mashup Score: 71
In this editorial, the authors describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder.
Source: www.nejm.orgCategories: General Medicine News, General Journals & SocietTweet-
In a new editorial, @AndreaGropman, MD, and Alexis C. Komor, PhD (@KomorLab), describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder. Read the editorial: https://t.co/DGBBKbEX2r #ASGCT2025 | @ASGCTherapy https://t.co/Uq6WY3uQix
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Presented at #ASGCT2025: A lipid nanoparticle–delivered base-editing therapy was custom designed for an infant with a ureacycle disorder. The affected infant was treated at approximately 7 and 8 months of age. Read the Brief Report: https://t.co/EtnnBhGfqi Editorial: https://t.co/56A43OZuy2