Aquestive Therapeutics’ Clinical Pipeline (ALS, LGS, Epilsepsy) | CheckRare.com
Aquestive Therapeutics is a specialty pharmacy company that is highly focused on providing treatment options for persons unable to properly swallow medicine.
Aquestive Therapeutics is a specialty pharmacy company that is highly focused on providing treatment options for persons unable to properly swallow medicine.
Erdheim-Chester disease is a rare condition affecting many parts of the body, it most commonly affects adults.
Jean Elwing discusses PAH research leading to better management of people with Pulmonary Arterial Hypertension
Anita D’Souza, MD, discusses results from the MajesTEC-2 and TRIMM-2 clinical trials for tec-DP in patients with multiple myeloma.
Drs. Aleena Banerji, Timothy Craig, and Marc Riedl, provide an overview of the discrepancies and discuss improving health equity in HAE.
Paula Ragan, X4 Pharmaceuticals, discusses the pathway of approval under the EMA for mavorixafor for patients with WHIM syndrome.
Dr Ozlem Goker-Alpan and Dr John Bach discuss best practices to manage pulmonary symptoms in lysosomal diseases
Emma Searle, PhD, discusses bleximenib in combination with chemotherapy to treat patients with acute myeloid leukemia (AML).
Yuliya Linhares, MD, Chief of Lymphoma Services at Miami Cancer Institute, discusses strategies for shortening the diagnostic journey of CTCL.
Jean Donadieu, MD Service d’Hémato-Oncologie Pédiatrique, Hopital, Paris, provides an overview of WHIM syndrome.
Larisa Geskin, MD, Columbia University Medical Center and Comprehensive Skin Cancer Center at the Division of Cutaneous Oncology in the Department of Dermatology, discusses the…